thalassemia refers specifically to the abnormal or absent manufacturing of alpha-globin chains. These are associated with more than 15 different genetic mutations. The severity of the clinical ...

Known as Zynteglo in Europe where it is approved to treat the rare blood disorder beta-thalassemia ... triggering a mutation or disrupting a mechanism that guards against a cell becoming cancerous.

It markets TRIKAFTA/KAFTRIO for people with CF with at least one F508del mutation for 2 years of ... cell disease and transfusion-dependent beta thalassemia which is in Phase 2/3 clinical trial.

More recently, Bluebird Bio’s Zynteglo (betibeglogene autotemcel), a cell-based gene therapy to treat transfusion-dependent beta-thalassemia ... in patients born with mutations in the gene ...

Apple Intelligence has been the focus of most iOS 18 updates so far, and we’re still waiting on the big Siri overhaul that adds personal context using the data on your phone and scores of new ...

After hours: January 24 at 7:49:33 p.m. EST ...

Genetics is the branch of science concerned with genes, heredity, and variation in living organisms. It seeks to understand the process of trait inheritance from parents to offspring, including ...