Cystoid macular edema (CME) is a condition characterized by the accumulation of fluid in the macula, leading to swelling and potential vision impairment. This condition can occur as a side effect ...
Presa, Bailey et al. assess the feasibility and efficacy of intrathecal administration of AAV9-SUMF1 gene therapy in the Sumf1-KO mouse model of Multiple Sulfatase Deficiency. They show that it ...