Hair serves an important cosmetic function for humans, and the hair follicle produces sweat gland products that help to control body temperature and release pheromones 3. Billions of people ...

Researchers at Washington University School of Medicine in St. Louis have described the neurodegeneration that occurs in the ...

Only a few patients have undergone an intensive gene therapy cure for sickle cell disease since it was approved by the FDA due to it's high cost and limited access.

But “as it is currently formulated, you can only get gene therapy once,” said Adam Cuker ... the proteins that help blood clots form. The subcutaneous injection drug emicizumab (Hemlibra ...

Today, gene therapy has broader applications, with trials covering many clinical problems including genetic diseases, cancer, infections such as HIV, and degenerative diseases. The transfer of genetic ...

"Our study shows that we can deliver genes to renal tubules and podocytes [highly specialized cells] in the kidney, the two important target cell types for gene therapy, and while there is a ...

Joe DePinto, MBA, discussed the findings of the McKesson 2024 Cell and Gene Therapy Report, providing insight into the challenges and opportunities in equitable access to these treatments.

Spark Therapeutics is on the cusp of gaining the first ever approval for a gene therapy from the FDA ... about creative payment models? No thanks; can we talk about your haemophilia drug?” ...

New developments in regenerative medicine are providing alternative solutions that aim to address the underlying issues of ...

CRISPR is a powerful gene-editing tool that holds enormous potential for treating genetic diseases by allowing scientists to ...

“Our study shows that we can deliver genes to renal tubules and podocytes [highly specialized cells] in the kidney, the two important target cell types for gene therapy, and while there is a ...