uniQure says it has reached an agreement with the FDA on a pathway to accelerated approval for its Huntington's disease gene therapy based on a phase 1/2 trial. The announcement led to a doubling ...

In gene therapy, a person's faulty genes are either replaced or modified ... However, SV-AUC was better than SEC-MALS in creating a detailed "map" of the distribution of the genetic and viral ...

Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and accurate ...